In the pivotal study, AQNEURSA improved neurological symptoms and showed functional benefits that could be seen within 12 weeks when compared with responses to placebo.1,*
To discover more about AQNEURSA, review the Full Prescribing Information.
The AQNEURSA Cares program can help eligible patients access treatment.
Learn more by downloading the brochure that's right for you:
AQNEURSA™ (levacetylleucine) is indicated for the treatment of neurological manifestations of Niemann-Pick disease type C (NPC) in adults and pediatric patients weighing ≥15 kg.
Do not take AQNEURSA if you:
Before taking AQNEURSA, discuss with your doctor if you:
The most common side effects of AQNEURSA include abdominal pain, dysphagia, upper respiratory tract infections and vomiting. Speak with your doctor if these side effects persist or worsen.
Take AQNEURSA exactly as prescribed by your doctor.
If a dose of AQNEURSA is missed, skip the missed dose and take the next dose at the scheduled time. Do not take 2 doses at the same time to make up for a missed dose.
AQNEURSA can be taken with or without food.
You are encouraged to report negative side effects of prescription drugs to the FDA. Visit www.fda.gov/medwatch, or call 1-800-FDA-1088.
Please click here for Full Prescribing Information for AQNEURSA.